Base editing in infants: Personal gene therapy on request:
A CPS1 deficiency is a rare, life-threatening, autosomal recessive disorder of the urea cycle ...
pharmazeutische-zeitung.de/persoenliche-gentherapie-auf-bestellung-156000/
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genetic modification of a patient's cells to produce a therapeutic effect
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New genome editing method could swap entire genes and correct 1000 mutations at once
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The Push for Artificial Inheritance: Experts worry about the risks of editing genes in human embryos. New startups seem poised to throw caution to the wind.
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Three technologies that will shape biotech in 2026: Why personalized gene editing, genetic resurrections and embryo scoring made our list.
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Baby KJ’s gene-editing treatment lands him on Nature’s top 10 list: Ongoing clinical trials at CHOP and Penn are testing ways to make the bespoke treatment ...
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New gene-editing tech repurposes bacterial retrons to correct large stretches of DNA
phys.org/news/2025-10-gene-tech-repurposes-bacterial-retrons.html
How tailored genetic therapy offers hope for rare disorders: Advances in genome editing are transforming the treatment for rare genetic diseases ...
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Baby Given World-First CRISPR Gene-Editing Treatment: In a global first, doctors have used personalized CRISPR gene-editing to treat a baby with a ...
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CPS-1 deficiency: Infant treated with gene therapy for the first time: For the first time, an infant with the rare metabolic disorder CPS1 deficiency has been ...
ptaheute.de/aktuelles/2025/06/05/cps-1-mangel-saeugling-erstmals-mit-gentherapie-behandelt
Baby KJ leaves CHOP after 307 days thanks to novel gene-editing therapy: KJ Muldoon's life-threatening disorder, called severe carbamoyl phosphate synthetase 1 ...
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Personalized gene editing saved a baby, but the tech’s future is uncertain: The personalized CRISPR treatment could be the future of gene therapy ...
sciencenews.org/article/personalized-crispr-gene-edit-therapy
"This is revolutionary": What personalized gene therapy means for those affected: In the USA, a baby was successfully treated with personalized gene therapy for ...
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Breakthrough in gene therapy: Infant with rare disease successfully treated: Incurable diseases could be combated with this promising therapy ...
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Infant becomes world's first patient to undergo personalized gene-editing treatment
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Doctors successfully treated a baby with the first ever personalized gene-editing therapy
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The genetic mystery of why some people develop autism: Genetic factors are thought to play a major role in the development of autism – but for decades what they ...
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Precision gene therapy for liver disorders increases number of correctly repaired cells
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Beyond gene-edited babies: the possible paths for tinkering with human evolution: CRISPR will get easier and easier to administer. What does that mean for the ...
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