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Shionogi to buy US-based IntraBio for $2bn to expand rare disease drug business: OSAKA/TOKYO -- Japanese drugmaker Shionogi will acquire U.S.-based biopharma ...
asia.nikkei.com/business/pharmaceuticals/shionogi-to-buy-us-based-intrabio-for-2bn-to-expand-rare-disease-drug-business

Regeneron drug for disease that causes dangerous bone growth earns FDA approval: Patients with FOP form bone where it shouldn't be. The drug, Pasatru ...
statnews.com/2026/08/19/regeneron-fop-garetosmab-fda-approval-pasatru/

Paid articlePaywallNursing Practice in Rare Disease: Care Coordination: How can you reduce fragmentation of care, shorten diagnostic journeys, improve outcomes for patients ...
medscape.org/viewarticle/nursing-practice-rare-disease-care-coordination-2025a1000uqe
Rett syndrome is often labeled a "childhood disease," but the data says otherwise.
With 70%+ of patients now living into their 50s and beyond ...
x.com/i/broadcasts/1YpJkkBNzXVJj

Nursing Practice in Rare Disease: Care Coordination: How can you reduce fragmentation of care, shorten diagnostic journeys, improve outcomes for patients ...
medscape.org/viewarticle/nursing-practice-rare-disease-care-coordination-2025a1000uqe
Study of rare bone disease reaches important milestone: Progress by a UMass Chan Medical School researcher in developing a gene therapy for a rare ...
medicalxpress.com/news/2022-10-rare-bone-disease-important-milestone.html

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